SUN-334 Real-World Clinical Profiles of Adults with Hypophosphatasia (HPP) from the Global HPP Registry
To read more please click on the link below.
Read Article
Related Articles
Hypophosphatasia. Nature’s Window on Alkaline Phosphatase Function in Humans
To read more please click on the link below. Read Article
Patient of the Month- Carol L.
My HPP story started at a very young age. I was quite young and our bedroom was upstairs, and the bathroom was downstairs. I would…
SUN-349 Characterizing Functional Performance in Adults with Hypophosphatasia
To read more please click on the link below. Read Article
Burden of Illness in Adults With Hypophosphatasia: Data From the Global Hypophosphatasia Patient Registry
To read more please click on the link below. Read Article
Use of real‐world evidence in regulatory decisions for rare diseases in the United States—Current status and future directions
To read more please click on the link below. Read Article
Responses