Patient of the Month- Ryan
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Tag: hypophosphatasia
Patient of the Month- Nikki W.
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Key Learnings from Clinical Research and Real World Evidence on Asfotase Alfa Effectiveness in Hypophosphatasia10 Years Post-Approval
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Medical Management of Hypophosphatasia: Review of Data on Asfotase Alfa (March, 2025) Kathryn McCrystal Dahir and Nancy S. Dunbar
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Patient of the Month- Cleo H.
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Patient of the Month- Alison S.
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Patient of the Month- Amedie P.
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Whole genome sequencing in adults with clinical hallmarks of hypophosphatasia negative for ALPL variants
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Safety, pharmacokinetics, and pharmacodynamics of efzimfotase alfa, a second-generation enzyme replacement therapy: phase 1, dose-escalation study in adults with hypophosphatasia
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Prevalence of chondrocalcinosis and calcium pyrophosphate deposition disease in a cohort of adult patients with low alkaline phosphatase levels and a positive versus negative genetic ALPL study
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