• About WordPress
    • WordPress.org
    • Documentation
    • Support
    • Feedback
  • Log In
  • Events
    • View Calendar
  • DONATE
  • HPP at a Glance
  • Soft Bones Resources
    • Fact Sheets
    • Brochures
    • Webinars
    • Podcasts
    • Newsletters
    • Patient Stories
    • Children
    • Be Prepared
  • Scientific Publications
  • HPP News
Soft Bones Logo
  • Programs and Services
    • Patient Support
    • Youth and Teen
    • Physician Support
    • Patient Education
    • Policy and Partnerships
  • HPP Community
    • Bone Zone
    • HPP AND ME
    • Photo Gallery
  • Newly Diagnosed?
  • Research
  • Get Involved
    • Calendar of Events
    • Soft Bones Store
    • Volunteer
    • Ways to Donate
    Sign in
    • Programs and Services
      • Patient Support
      • Youth and Teen
      • Physician Support
      • Patient Education
      • Policy and Partnerships
    • HPP Community
      • Bone Zone
      • HPP AND ME
      • Photo Gallery
    • Newly Diagnosed?
    • Research
    • Get Involved
      • Calendar of Events
      • Soft Bones Store
      • Volunteer
      • Ways to Donate

    • DONATE
    • HPP at a Glance
    • Soft Bones Resources
      • Fact Sheets
      • Brochures
      • Webinars
      • Podcasts
      • Newsletters
      • Patient Stories
      • Children
      • Be Prepared
    • Scientific Publications
    • HPP News

    Tag: Gene therapy

    Aruvant Announces ARU-2801 Data Presentations at the American Society for Bone and Mineral Research (ASBMR) 2021 Annual Meeting

    To read more please click the link below. View News Article

    Denise Goodbar September 22, 2021
    0 Comments

    Successful treatment with bone maturation and average life expectancy of hypophosphatasia model mice by adeno-associated virus type 8-mediated neonatal gene therapy via single muscle injection

    To read more please click on the link below. Read Article

    Denise Goodbar June 14, 2021
    0 Comments

    Study supports gene therapy as a promising treatment for soft bone disease

    To read more please click the link below. View News Article

    Denise Goodbar June 7, 2021
    0 Comments

    Genetic correction of induced pluripotent stem cells mediated by transcription activator-like effector nucleases targeting ALPL recovers enzyme activity and calcification in vitro

    To read more please click on the link below. Read Article

    softbones October 28, 2020
    0 Comments
    • Facebook
    • Instagram
    June 2023
    M T W T F S S
     1234
    567891011
    12131415161718
    19202122232425
    2627282930  
    « May    
    • Childrens Resources
    • Emergency
    • Fact Sheets
    • HPP Stories
    • News
    • Newsletters
    • Podcasts
    • Scientific Publications
    • Soft Bones Publications
    • Translated Soft Bones Publications
    • Uncategorized
    • Webinars

    The US Hypophosphatasia Foundation
    141 Hawkins Place, #267
    Boonton, NJ 07005, USA.

    • Local: (973) 453-3093
    • Toll Free: (866) 827-9937
    • info@softbones.org

    Organization

    • About Soft Bones
    • Fundraising
    • Soft Bones Store
    • About Soft Bones
    • Fundraising
    • Soft Bones Store

    Programs

    • Patient Education
    • Patient Support
    • Physician Education
    • Patient Education
    • Patient Support
    • Physician Education

    Community

    • Bone Zone
    • HPP AND ME
    • Get Involved
    • Bone Zone
    • HPP AND ME
    • Get Involved
    GET INVOLVED
    Instagram Twitter Facebook Linkedin Youtube Pinterest