Hypophosphatasia—pathophysiological understanding, preclinical data looking beyond the skeleton, and upcoming treatments
To read more please click on the link below. Read Article
Tag: Gene therapy
Aruvant Announces ARU-2801 Data Presentations at the American Society for Bone and Mineral Research (ASBMR) 2021 Annual Meeting
To read more please click the link below. View News Article
Successful treatment with bone maturation and average life expectancy of hypophosphatasia model mice by adeno-associated virus type 8-mediated neonatal gene therapy via single muscle injection
To read more please click on the link below. Read Article
Study supports gene therapy as a promising treatment for soft bone disease
To read more please click the link below. View News Article
Genetic correction of induced pluripotent stem cells mediated by transcription activator-like effector nucleases targeting ALPL recovers enzyme activity and calcification in vitro
To read more please click on the link below. Read Article